2026 NORD Rare Diseases and Orphan Products Breakthrough Summit
Advancing rare disease therapies requires connecting scientific strategy with significant patient realities. At Syneos Health®, we bring together clinical, regulatory and patient engagement expertise to help sponsors design and deliver programs around those realities.
Meet with our rare disease experts at the National Organization for Rare Disorders (NORD)’s annual Rare Diseases and Orphan Products Breakthrough Summit to discuss your next development challenge.
A development plan must account for how patients access specialized care, how caregivers support participation and what sites need to deliver a study. These considerations shape decisions from protocol design and site selection through recruitment, retention and long-term follow-up. We help sponsors address those connections across rare and ultra-rare disease programs.
- Connect Patients With Study Opportunities: Reach small, dispersed populations through specialized sites, investigators, centers of excellence and patient advocacy relationships. Our global capabilities and therapeutic expertise support recruitment strategies informed by where patients receive care and how they learn about research.
- Make Participation More Manageable: Consider the demands on patients, caregivers and families early in planning. We help sponsors incorporate travel support, patient concierge services, home health solutions and decentralized approaches where appropriate for the study and population.
- Align Scientific Strategy With Trial Delivery: Bring medical, regulatory, operational and patient engagement expertise together to assess development decisions. Our multidisciplinary teams help sponsors build strategies that account for scientific objectives, regulatory requirements and the practical demands of execution.
- Plan for What Comes Next: Connect early development choices with later milestones, including regulatory submissions, long-term follow-up and commercialization readiness. Our integrated perspective helps sponsors consider the evidence and support their programs may need as development progresses.
- Expertise Across Complex Rare Disease Programs: Our teams bring experience across rare, pediatric and specialty disease programs, spanning traditional therapies, biologics and cell and gene therapies. We connect that expertise with global trial delivery capabilities and patient and caregiver support services.
Request a meeting with our rare disease experts at this year’s NORD Rare Diseases and Orphan Products Breakthrough Summit.
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